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Transgenic mouse model
Cell therapy
Aged
Myotonic dystrophy
Dilated cardiomyopathy
PABPN1
Rare diseases
Glutamate
Myopathy
Calcium
Laminopathies
RNA interference
Neuromuscular disease
Genotype phenotype correlation
Heart failure
Myasthenia Gravis MG
Neuromuscular junction
Biomarker
Brain
Treatment
Myotonic Dystrophy
Cancer
Trinucleotide repeat expansion
Laminopathie
MBNL
Dystrophin
Mouse model
Autoantibodies
Antisense oligonucleotides
Duchenne muscular dystrophy
Lamin A/C
CMS
Satellite cells
Alternative splicing
Myopathies
Astrocyte
LMNA
Therapy
Myoblasts
Muscle
Centronuclear myopathy
COVID-19
CRISPRi
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Actin
Lamin A/C LMNA gene
Becker muscular dystrophy
Satellite cell
Myotonic dystrophy type 1
Gene therapy
DMD
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Motoneuron
Laminopathy
Cytokines
Autophagy
ALS
Myotonic Dystrophy type 1
Heart
Outcome measures
Rare neuromuscular diseases
Myogenesis
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Dynamin 2
Exercise
Thymus
Skeletal muscle
Male
Thérapie génique
Cytoskeleton
Muscle regeneration
Animals
CTG repeat contractions
Errance diagnostique
Fabry disease
Cardiomyopathy
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Amyotrophic lateral sclerosis
RNA biology
AAV
Clinical trials
Congenital muscular dystrophy
Congenital myopathy
Regeneration
Transcriptomics
Biomarkers
Autoimmunity
OPMD
Long read sequencing
Aging
Myasthenia gravis
LMNA gene
Inflammation
Neuromuscular diseases
Nuclear envelope
Muscular dystrophy
Mechanotransduction
Humans
Myositis